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Advancing gene targeting for primary immune deficiencies: Adenine base editing of the human IL2RG locus for correction of SCID-X1.

McIvor RS, Eaton EJ, Webber BR, Moriarity BS

Molecular therapy : the journal of the American Society of Gene Therapy, 32(6): 1606-1608 PMID 38781958 DOI 10.1016/j.ymthe.2024.05.026