Gene Editing Successfully Corrects 2 Amino Acid Disorders: In 2 preclinical studies using CRISPR-mediated gene editing, phenylketonuria and hereditary tyrosinemia type 1 were corrected.
American journal of medical genetics. Part A, 179(1): 5-6 PMID 30681273 DOI 10.1002/ajmg.a.61026
Abstract
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